Drug Delivery System for Niemann Pick Type C1 Disease Discovered
NPC1 affects about one in every 120,000 children globally and results in abnormal cholesterol accumulation, progressive neurodegeneration and death.
NPC1 affects about one in every 120,000 children globally and results in abnormal cholesterol accumulation, progressive neurodegeneration and death.
Gene Therapy Brings Hope for Bubble Boy Disease Treatment
Gene therapy by GlaxoSmithKline offers hope for children with bubble boy disease with Phase I and II approved by EU regulation board.
Gene therapy by GlaxoSmithKline offers hope for children with bubble boy disease with Phase I and II approved by EU regulation board.