The Spinal Muscular Atrophy (SMA) Foundation has announced the launch of a pilot study of Biomarkers for Spinal Muscular Atrophy (BforSMA). The Foundation is a nonprofit organization dedicated to accelerating the development of a treatment for SMA.
The goal of this study is to identify a potential biomarker or panel of biomarkers that can be used as objective measures of SMA disease severity. The identification of such biomarkers may help to assess drug efficacy and shorten the duration of clinical trials.
Cervical Spondylosis - Causes - Symptoms - Diagnosis - Treatment - FAQs
Cervical spondylosis is a disorder in which there is abnormal wear on cervical vertebrae.
Cervical spondylosis is a disorder in which there is abnormal wear on cervical vertebrae.
"The SMA Foundation is taking a bold initiative to identify markers of disease severity in spinal muscular atrophy,” noted Richard Finkel, MD, a principal investigator for the trial at the Children’s Hospital of Philadelphia. “The team of SMA clinicians is eager to partner with experienced industry pioneers, including BG Medicine and NERI, towards realizing this goal. Having such biomarkers will greatly enhance the development of new and novel therapies for this disabling disorder."
Cynthia Joyce, Executive Director for the SMA Foundation, added, “This pilot project has the potential to be a landmark study for therapeutics development – rapid completion will help make future clinical trials more efficient and more informative.
Meningitis - Causes - Symptoms - Diagnosis - Treatment - FAQs
Meninges are the three layers of membrane that cover the brain and infection of the cerebrospinal fluid between them causes meningitis the disease of the meninges.
Meninges are the three layers of membrane that cover the brain and infection of the cerebrospinal fluid between them causes meningitis the disease of the meninges.
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Innovative Technique can End Chronic Pain Without Drugs
Two pain management specialists, including one of Indian origin, have come up with a technique that can help end chronic back and leg pain - without the need of taking drugs.
Two pain management specialists, including one of Indian origin, have come up with a technique that can help end chronic back and leg pain - without the need of taking drugs.
Stem Cells may Act as Mediators in Gene Therapy to Injured Nervous System
American researchers have found that transplanted bone marrow stem cells can attach themselves to injured areas in the brain or spinal cord.
American researchers have found that transplanted bone marrow stem cells can attach themselves to injured areas in the brain or spinal cord.
